-
Voretigene neparvovec, sold
under the
brand name Luxturna, is a gene
therapy medication for the
treatment of
Leber congenital amaurosis. Leber's congenital...
-
December 2017, the U.S. Food and Drug
Administration approved Luxturna (
voretigene neparvovec-rzyl) for the
treatment of
patients with
viable retinal cells...
-
alipogene tiparvovec (2012),
Strimvelis (2016),
tisagenlecleucel (2017),
voretigene neparvovec (2017),
patisiran (2018),
onasemnogene abeparvovec (2019),...
- Æterna (film), a 2019 film
directed by
Gaspar Noé Luxturna,
trade name for
voretigene neparvovec, a gene
therapy for the
treatment of Leber's
congenital amaurosis...
- INN)
vorasidenib (INN)
Voraxaze voreloxin (USAN, INN)
voretigene neparvovec (USAN, INN)
voretigene neparvovec-rzyl
voriconazole (INN)
vorinostat (USAN)...
- needed] On 19
December 2017, the U.S. Food and Drug
Administration approved voretigene neparvovec-rzyl (Luxturna), an adeno-****ociated
virus vector-based gene...
- (ranibizumab), for wet age-related
macular degeneration (AMD).
Luxturna (
voretigene neparvovec), for Leber's
congenital amaurosis.
MabThera (rituximab), for...
-
amaurosis RPE65
Subretinal I–II
Multiple Several ongoing and
complete (
voretigene neparvovec) Age-related
macular degeneration sFlt-1
Subretinal I–II 24...
- to see in
black and white. In 2017 the FDA
approved the gene
therapy voretigene neparvovec to
treat people with
biallelic RPE65 mutation-****ociated retinal...
- 2012, in 2017, the FDA
approved the
first AAV-based in vivo gene therapy—
voretigene neparvovec—which
treated RPE65-****ociated
Leber congenital amaurosis....
