Definition of Risdiplam. Meaning of Risdiplam. Synonyms of Risdiplam

Here you will find one or more explanations in English for the word Risdiplam. Also in the bottom left of the page several parts of wikipedia pages related to the word Risdiplam and, of course, Risdiplam synonyms and on the right images related to the word Risdiplam.

Definition of Risdiplam

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Meaning of Risdiplam from wikipedia

- Risdiplam, sold under the brand name Evrysdi, is a medication used to treat spinal muscular atrophy (SMA) and the first oral medication approved to treat...
- Medications that target the genetic cause of the disease include nusinersen, risdiplam, and the gene therapy medication onasemnogene abeparvovec. Supportive...
- diagnosed at birth. In 2020, PTC announced the FDA approval of Evrysdi (risdiplam) for the treatment of spinal muscular atrophy (SMA) in adults and children...
- Nusinersen M09AX08 Golodirsen M09AX09 Onasemnogene abeparvovec M09AX10 Risdiplam M09AX11 Palovarotene M09AX12 Viltol****n M09AX13 Casimersen M09AX14 Givinostat...
- trials (NCT06118086, NCT06297941). The splicing modulator small molecule risdiplam, originally developed to promote exon 7 inclusion in the SMN2 transcript...