Definition of Golodirsen. Meaning of Golodirsen. Synonyms of Golodirsen

- Golodirsen, sold under the brand name Vyondys 53, is a medication used for the treatment of Duchenne muscular dystrophy. It is an antisense oligonucleotide...
- M09AX05 Aceneuramic acid M09AX06 Eteplirsen M09AX07 Nusinersen M09AX08 Golodirsen M09AX09 Onasemnogene abeparvovec M09AX10 Risdiplam M09AX11 Palovarotene...
- targeting exon 51 of human dystrophin. Another exon-skipping Morpholino, golodirsen (Vyondys 53) (targeting dystrophin exon 53), was approved in the United...
- was approved for medical use in the United States in August 2020. After golodirsen was approved in December 2019, viltol****n is the second approved targeted...
- approved for use in the European Union. The antisense oligonucleotide golodirsen (Vyondys 53) was approved for medical use in the United States in 2019...
- Following the approval of eteplirsen, two other drugs of a similar kind, golodirsen and viltol****n received provisional approval from the FDA for the treatment...
- Heasman using Xenopus. FDA-approved Morpholino drugs include eteplirsen and golodirsen. The antisense oligonucleotides have also been used to inhibit influenza...
- from skipping exon 51 of the dystrophin transcript. In December 2019, golodirsen (Vyondys 53) received FDA approval for the treatment of cases that can...
- approval process was mired in controversy. Other Morpholino-based drugs golodirsen, viltol****n, and casimersen (also for Duchenne muscular dystrophy) were...
- studies when the drug was given by intravenous injection. In December 2019, golodirsen (Vyondys 53) received US FDA approval for the treatment of cases that...